@article{Maguire2008gene,
  author = {Maguire and Simonelli and Pierce and others},
  title = {Safety and Efficacy of Gene Transfer for Leber's Congenital Amaurosis},
  journal = {New England Journal of Medicine},
  year = {2008},
  doi = {10.1056/NEJMoa0802315},
  url = {https://doi.org/10.1056/NEJMoa0802315}
}

@article{Russell2017voretigene,
  author = {Russell and Bennett and Wellman and others},
  title = {Efficacy and safety of voretigene neparvovec (AAV2-hRPE65v2) in patients with RPE65 -mediated inherited retinal dystrophy: a randomised, controlled, open-label, phase 3 trial},
  journal = {The Lancet},
  year = {2017},
  doi = {10.1016/S0140-6736(17)31868-8},
  url = {https://doi.org/10.1016/S0140-6736(17)31868-8}
}

@article{Mendell2017gene,
  author = {Mendell and Al-Zaidy and Shell and others},
  title = {Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy},
  journal = {New England Journal of Medicine},
  year = {2017},
  doi = {10.1056/NEJMoa1706198},
  url = {https://doi.org/10.1056/NEJMoa1706198}
}

@article{Wang2019aav,
  author = {Wang and Tai and Gao},
  title = {Adeno-associated virus vector as a platform for gene therapy delivery},
  journal = {Nature Reviews Drug Discovery},
  year = {2019},
  doi = {10.1038/s41573-019-0012-9},
  url = {https://doi.org/10.1038/s41573-019-0012-9}
}